Patients with ALGS treated with maralixibat in a real-world analysis had lower rates of adverse events (AEs) than described in clinical trials, according to data presented at The Liver Meeting of the American...

Most patients diagnosed with inherited retinal diseases (IRDs) opt to undergo genetic testing to gather information for their relatives, according to a study. Researchers asked 132 patients diagnosed with IRDs treated at an...

Treatment with teprotumumab is associated with a reduction in intraocular pressure (IOP) in patients with thyroid eye disease (TED), according to a study. In this retrospective review, the IOP, extent of proptosis, and...

The efficacy of once-weekly somatrogon was comparable to once-daily somatropin in prepubertal children with growth hormone deficiency (GHD), according to a study. In this phase 3, open-label, randomized trial, children with GHD were randomized...

Due to the large number of patients with rheumatoid arthritis (RA) who suffer with RA-associated interstitial lung disease (ILD), routine screening is needed to identify pulmonary involvement, according to a study. In this...