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Conference Roundup

From Concept to Clinical Trial: Developing Treatments for Rare Diseases

From basic research through drug discovery, preclinical work in animals, clinical trials in humans, and then regulatory approval, therapeutic development is an often complicated, controlled process said Lara Longpre, Chief Development Officer at Mirum Pharmaceuticals during a presentation at the 2023 PFIC Family & Scientific Conference. “This looks like a...

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